2023 · pending · WO2025137323A1
Treatment of CPN1 Related Diseases and Disorders
Gregory McInnes
Compositions comprising oligonucleotides (siRNA or ASO) that target CPN1 for treating conditions associated with CPN1 gene mutations.
RNA Therapeutics
2023 · pending · WO2025137323A1
Gregory McInnes
Compositions comprising oligonucleotides (siRNA or ASO) that target CPN1 for treating conditions associated with CPN1 gene mutations.
RNA Therapeutics